NPC Research Topics Index
Niemann-Pick Disease Type C (NPC) Research Topics
Index of Posts
This page provides an index of posts made to the NNPDF Web site’s Latest Research page (and occasionally, other pages) regarding Niemann-Pick Disease Type C (NPC). Posts include research studies, papers, clinical trials, and other research topics of interest to those affected by NPC.
The posts are listed in reverse chronological order, with the most recent post at the top of the list. Key words are provided to help you locate the information you need, and a direct link is provided for the most recent postings, as well. For older items (those farther down the list below), copy and paste the URL into your browser's address bar, and when you arrive at the Web page, scroll down to the date of the posting you seek.
We strive to keep the NNPDF Web site up-to-date with the latest and most accurate information, and to make it as easy as possible for users to locate information. The Web site is always growing, and the number of visitors and resultant inquiries tells us it serves as an important reference for those affected by Niemann-Pick Disease around the world.
Each posting listed below has a date associated with it; older articles are maintained for archival purposes. Please keep in mind that some of the articles and postings are historical, and older information may have been superseded by more recent research or announcements. If you have questions about the information, please contact the NNPDF or ask your physician for clarification.
We would also appreciate if you would let us know if you have ideas to make our Web site even better, or if you encounter any broken links, etc. Thank you!
Contact the NNPDF
Additional tools to help you navigate the NNPDF site and find the information you need:
Picosearch -- enter your search term in the Picosearch box in the left margin of every page on our site, click "Go," and you will see a list of pages containing the term
Index page -- Use this site index, where Web pages are grouped by general topic, to help you locate information on this site.
| Date Posted | Item | Key Words | Link to Post or URL |
| 4/7/11 | NIH to Develop Clinical Trial with Cyclodextrin | NPC, cyclodextrin, NIH, TRND, clinical trial | |
| 4/5/11 | Paper Published on Study of Histone Deacetylase Inhibitor for Use in NPC | Histone deacetylase inhibitor, HCAD inhibitor, valproic acid, NPC, Notre Dame | http://www.nnpdf.org/npdisease_14.html |
| 3/17/11 | Webinar with NIH Director Dr. Francis Collins about the Proposed National Center for Advancing Translational Sciences (NCATS) | Rare diseases, NCATS, NIH, Collins, Webinar, Faster Cures, orphan drugs | http://www.nnpdf.org/npdisease_14.html |
| 3/9/11 | 2011 Peter G. Pentchev Postdoctoral Fellowships Request for Applications | Research, funding, postdoctoral, fellowship, application, NPC | http://www.nnpdf.org/npdisease_14.html |
| 3/2/11 | RRD International Selected as Development Partner for NIH TRND Program: Focus on NPC1 |
RRD, TRND, NIH, new drugs for rare diseases | http://www.nnpdf.org/npdisease_14.html |
| 2/25/11 | NPC Research Updates from Dr. Dan Ory, Scientific Advisory Board Chair | NPC, research, updates | http://www.nnpdf.org/npdisease_14.html |
| 1/25/11 | New Test Promises to Find Fatal Diseases Before Conception | Genetics, inherited diseases | http://www.nnpdf.org/npdisease_14.html |
| 12/9/10 | NIH Rare Diseases Clinical Research Network (RDCRN) | NIH, RDCRN, rare disease support | http://www.nnpdf.org/npdisease_14.html |
| 12/9/10 | Rare Diseases Clinical Research Network E-Newsletter | RDCRN, NIH | http://www.nnpdf.org/npdisease_14.html |
| 11/19/10 | Oxidative Stress in NPC | Oxidative stress | http://www.nnpdf.org/npdisease_14.html |
| 11/12/10 | Updates from Research Fellows | Peter Pentchev Fellowships | http://www.nnpdf.org/npdisease_14.html |
| 11/4/10 | NPC May Soon be Diagnosed via Blood Test | Diagnostics, blood test | http://www.nnpdf.org/npdisease_14.html |
| 10/14/10 | Ara Parseghian Medical Research Foundation (APMRF) Conference | APMRF | http://www.nnpdf.org/npdisease_14.html |
| 10/4/10 | Institute of Medicine (IOM) Report on Rare Diseases | IOM, rare diseases | http://www.nnpdf.org/npdisease_14.html |
| 9/14/10 | 2010 Pentchev Fellowships Awarded | Pentchev, research, fellowships | http://www.nnpdf.org/npdisease_14.html |
| 9/1/10 | Hearing on Rare and Neglected Pediatric Diseases | US Senate, rare diseases | http://www.nnpdf.org/npdisease_14.html |
| 7/9/10 | Promising Therapies for NPC - NINDS Meeting June 2010 | NINDS, NPC | http://www.nnpdf.org/npdisease_14.html |
| 6/9/10 | Niemann-Pick Type C Pathogenesis and Treatment: From Statins to Sugars |
Madra, Sturley, NPC | http://www.nnpdf.org/npdisease_14.html |
| 5/25/10 | FDA grants “Orphan Drug Designation” to Cyclodextrin for treatment of Niemann-Pick Disease Type C |
FDA, cyclodextrin | http://www.nnpdf.org/npdisease_14.html |
| 4/15/2010 | Are Stem Cells or Gene Replacement Viable Therapies for NPC? | Dr. Dan Ory, stem cells | http://www.nnpdf.org/npdisease_14.html |
| 3/17/2010 | Report from 2010 WORLD Meeting | Cate Walsh Vockley | http://www.nnpdf.org/npdisease_14.html |
| 3/5/2010 | NIH and FDA Announce Collaborative Initiative - Partnership to Speed New Treatments to Patients |
NIH, FDA | http://www.nnpdf.org/npdisease_14.html |
| 1/13/2010 | United States FDA Advisory Committee Backs Use of Zavesca for NPC |
FDA, Zavesca | http://www.nnpdf.org/npdisease_14.html |
| 12/21/2009 | More Details on Cyclodextrin from Dr. Dietschy's Lab |
Cyclodextrin | http://www.nnpdf.org/npdisease_14.html |
| 12/21/2009 | Adenovirus RID- |
Adenovirus, cholesterol | http://www.nnpdf.org/npdisease_14.html |
activates an autonomous cholesterol regulatory mechanism
that rescues defects linked to Niemann-Pick disease type C
The National Niemann-Pick Disease Foundation (NNPDF) does not engage in the practice of medicine. It is not a medical authority nor does it claim to have medical knowledge. This site is an educational service of the National Niemann-Pick Disease Foundation and is not meant to provide diagnostic or treatment advice. Information contained or suggested on this Web site does not constitute medical advice. For all information related to care, medication or treatment, the NNPDF recommends consulting a physician to determine if information presented is applicable. Please review these additional cautions about medical information provided on the Internet. This Web site is a service of the National Niemann-Pick Disease Foundation's Family Services Program, made possible by the financial support of our member families and other generous donors and grantors. This site receives no government funding, nor does it host or receive funding from advertising or from the display of commercial content. This site complies to the HONcode standard for trustworthy health information: verify here. The National Niemann-Pick Disease Foundation is a 501(c)(3) organization. Your donations are fully tax-deductible. |